Children's Hospital Association submitted comments on the cell and gene therapy request for information (RFI) from Sen. Bill Cassidy (R-La.), ranking member of the Senate Health, Education, Labor, and Pensions (HELP) Committee. Our response highlights the need to ensure children’s equitable access to these therapies and a strong national framework for payment and oversight.
CHA Response to Cell and Gene Therapy RFI
Cell and gene therapies have the potential to address unmet pediatric medical needs, reduce the need for costly chronic care, and help address health disparities.
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